Tag: ex vivo


  • Gene Therapy Shows Long-Term Success for Children with ADA-SCID

    Gene Therapy Shows Long-Term Success for Children with ADA-SCID

    Groundbreaking Study Highlights Long-Term Success of ADA-SCID Gene Therapy A landmark international study led by researchers from Great Ormond Street Hospital (GOSH), University College London (UCL), and the University of California, Los Angeles (UCLA) shows that gene therapy can provide durable, life-changing results for children with ADA-SCID, a rare and life-threatening immune deficiency. The team…